Lindsey George on Gene Therapy Transforming Hemophilia Care
The World Federation of Haemophilia (WFH) shared a post on X:
“Gene Therapy is changing the future of treatment for genetic disorders and AAV vectors are leading the way in delivering functional genes.
A new study looks at the current progress in clinical AAV gene therapy, including for hemophilia.”
AAV vectors are at the forefront of delivering functional genes, offering new hope for patients with genetic disorders — including hemophilia.
A new review by Lindsey George explores the current clinical applications of AAV-mediated gene therapy, highlighting advances and future directions.
Read the full article in Molecular Therapy Journal.
Article: Current clinical applications of AAV-mediated gene therapy
Authors: Barry J. Byrne, Kevin M. Flanigan, Susan E. Matesanz, Richard S. Finkel, Megan A. Waldrop, Eleonora S. D’Ambrosio, Nicholas E. Johnson, Barbara K. Smith, Carsten Bönnemann, Sean Carrig, Joseph W. Rossano, Barry Greenberg, Laura Lalaguna, Enrique Lara-Pezzi, Sub Subramony, Manuela Corti, Claudia Mercado-Rodriguez, Carmen Leon-Astudillo, Rebecca Ahrens-Nicklas, Diana Bharucha-Goebel, Guangping Gao, Dominic J. Gessler, Wuh-Liang Hwu, Yin-Hsiu Chien, Ni-Chung Lee, Sanford L. Boye, Shannon E. Boye, Lindsey George
Stay updated on all science in the field of hematology with Hemostasis Today.
-
Aug 26, 2026, 15:48Melissa Hollo: Postpartum Depression is More Than the “Baby Blues”
-
Aug 26, 2026, 15:46Raghavendra Rao: The Link Between Neuropathy and Chronic Venous Disease
-
Aug 26, 2026, 15:43Laurent Bertoletti: Long Term Benefits and Safety of Rehabilitation in Pulmonary Arterial Hypertension
-
Aug 26, 2026, 15:41Tamer Hellou: Chromosome 1q Gain Signals High Long-Term Risk in AL Amyloidosis
-
Aug 26, 2026, 15:04Sequential Efgartigimod and Eltrombopag Achieve Durable Response in Refractory ITP – Platelets Journal
-
Aug 26, 2026, 14:46Holly O’Byrne: A Framework for Developing and Managing Prehospital Blood Programs
-
Aug 26, 2026, 14:32Eleftherios Mylonakis: Earlier Intervention, Better Risk Stratification, Stronger BP Control
-
Aug 26, 2026, 14:32Bringing ISTH 2026 Research to the Global Scientific Community
-
Aug 26, 2026, 14:23Joseph R. Shaw: Thrombin Generation and the Pharmacodynamics of Oral Anticoagulants