Lindsey George on Gene Therapy Transforming Hemophilia Care
The World Federation of Haemophilia (WFH) shared a post on X:
“Gene Therapy is changing the future of treatment for genetic disorders and AAV vectors are leading the way in delivering functional genes.
A new study looks at the current progress in clinical AAV gene therapy, including for hemophilia.”
AAV vectors are at the forefront of delivering functional genes, offering new hope for patients with genetic disorders — including hemophilia.
A new review by Lindsey George explores the current clinical applications of AAV-mediated gene therapy, highlighting advances and future directions.
Read the full article in Molecular Therapy Journal.
Article: Current clinical applications of AAV-mediated gene therapy
Authors: Barry J. Byrne, Kevin M. Flanigan, Susan E. Matesanz, Richard S. Finkel, Megan A. Waldrop, Eleonora S. D’Ambrosio, Nicholas E. Johnson, Barbara K. Smith, Carsten Bönnemann, Sean Carrig, Joseph W. Rossano, Barry Greenberg, Laura Lalaguna, Enrique Lara-Pezzi, Sub Subramony, Manuela Corti, Claudia Mercado-Rodriguez, Carmen Leon-Astudillo, Rebecca Ahrens-Nicklas, Diana Bharucha-Goebel, Guangping Gao, Dominic J. Gessler, Wuh-Liang Hwu, Yin-Hsiu Chien, Ni-Chung Lee, Sanford L. Boye, Shannon E. Boye, Lindsey George
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