Lindsey George on Gene Therapy Transforming Hemophilia Care
The World Federation of Haemophilia (WFH) shared a post on X:
“Gene Therapy is changing the future of treatment for genetic disorders and AAV vectors are leading the way in delivering functional genes.
A new study looks at the current progress in clinical AAV gene therapy, including for hemophilia.”
AAV vectors are at the forefront of delivering functional genes, offering new hope for patients with genetic disorders — including hemophilia.
A new review by Lindsey George explores the current clinical applications of AAV-mediated gene therapy, highlighting advances and future directions.
Read the full article in Molecular Therapy Journal.
Article: Current clinical applications of AAV-mediated gene therapy
Authors: Barry J. Byrne, Kevin M. Flanigan, Susan E. Matesanz, Richard S. Finkel, Megan A. Waldrop, Eleonora S. D’Ambrosio, Nicholas E. Johnson, Barbara K. Smith, Carsten Bönnemann, Sean Carrig, Joseph W. Rossano, Barry Greenberg, Laura Lalaguna, Enrique Lara-Pezzi, Sub Subramony, Manuela Corti, Claudia Mercado-Rodriguez, Carmen Leon-Astudillo, Rebecca Ahrens-Nicklas, Diana Bharucha-Goebel, Guangping Gao, Dominic J. Gessler, Wuh-Liang Hwu, Yin-Hsiu Chien, Ni-Chung Lee, Sanford L. Boye, Shannon E. Boye, Lindsey George
Stay updated on all science in the field of hematology with Hemostasis Today.
-
Feb 25, 2026, 16:47Alan Nurden: Platelet Defects Explain Bleeding in EHDS Patients
-
Feb 25, 2026, 16:40Mohammed Almohammadi: Uniting Leaders in Laboratory Hematology at the 1st Saudi ISLH Joint Conference
-
Feb 25, 2026, 16:37Salihu Asimawu: Inflammation Is Not a Disease – Hats Off to the Heroes Inside Us
-
Feb 25, 2026, 16:34Michael Makris: Biomarin Has Decided to Withdraw Roctavian from the Market
-
Feb 25, 2026, 16:25Tagreed Alkaltham: The Blood Banker Personality
-
Feb 25, 2026, 16:17Sanjay Ahuja: Insightful Talk on 100 Years of VWD by Jorge Di Paola
-
Feb 25, 2026, 15:20Michael Shapiro։ Creating Real Pathways for Trainees in Preventive Cardiology
-
Feb 25, 2026, 15:15Ajay Kumar: Plasma Component Quality Control Standards
-
Feb 25, 2026, 15:09Wolfgang Miesbach: Efficacy, Safety and Thrombosis Signals in Haemophilia A/B with Inhibitors