Lindsey George on Gene Therapy Transforming Hemophilia Care
The World Federation of Haemophilia (WFH) shared a post on X:
“Gene Therapy is changing the future of treatment for genetic disorders and AAV vectors are leading the way in delivering functional genes.
A new study looks at the current progress in clinical AAV gene therapy, including for hemophilia.”
AAV vectors are at the forefront of delivering functional genes, offering new hope for patients with genetic disorders — including hemophilia.
A new review by Lindsey George explores the current clinical applications of AAV-mediated gene therapy, highlighting advances and future directions.
Read the full article in Molecular Therapy Journal.
Article: Current clinical applications of AAV-mediated gene therapy
Authors: Barry J. Byrne, Kevin M. Flanigan, Susan E. Matesanz, Richard S. Finkel, Megan A. Waldrop, Eleonora S. D’Ambrosio, Nicholas E. Johnson, Barbara K. Smith, Carsten Bönnemann, Sean Carrig, Joseph W. Rossano, Barry Greenberg, Laura Lalaguna, Enrique Lara-Pezzi, Sub Subramony, Manuela Corti, Claudia Mercado-Rodriguez, Carmen Leon-Astudillo, Rebecca Ahrens-Nicklas, Diana Bharucha-Goebel, Guangping Gao, Dominic J. Gessler, Wuh-Liang Hwu, Yin-Hsiu Chien, Ni-Chung Lee, Sanford L. Boye, Shannon E. Boye, Lindsey George
Stay updated on all science in the field of hematology with Hemostasis Today.
-
Nov 15, 2025, 15:47Shannon Farmer: Congratulations to Susan Goobie and Colleagues on Publication of Their Important Study
-
Nov 15, 2025, 15:46Fotios Barkas: Explore the Latest Articles From the Journal of Atherosclerosis Prevention and Treatment!
-
Nov 15, 2025, 15:45Ludovic Helfgott: Researchers Have Analysed Novo Nordisk Product Data in Obesity and Cardiovascular Disease
-
Nov 15, 2025, 15:42Haroun Gajraj Thanks Enric Roche for Demonstrating the Piston Effect
-
Nov 15, 2025, 15:41Thrombectomy Rates Rise 700% Nationwide
-
Nov 15, 2025, 15:41Emmanuel J. Favaloro: Transitioning Patients from DOACs to Heparin
-
Nov 15, 2025, 15:40Bruno Lima: I Owe a Lot of My Career to Dr. Brad Maron
-
Nov 15, 2025, 15:39Ramesh Balasubramanian: Future of Hematology is Encouraging. Striving Towards More Cure for the Dreaded Cancer
-
Nov 15, 2025, 15:37Atrial Fibrillation Increases the Risk of Stroke by Up to Fivefold Due to Clot Formation in the Atria