Patient Selection for Gene Therapy in Transfusion-Dependent β-Thalassemia – EHA
European Hematology Association (EHA) shared a post on LinkedIn about recent articles, adding:
“Who may benefit most from gene therapy in transfusion-dependent β thalassemia?
The updated EHA EBMT Consensus Report on Selecting Transfusion Dependent β Thalassemic Patients for Gene Therapy Approaches provides expert guidance to support patient selection and treatment decisions as gene therapy becomes part of routine clinical practice.
The report addresses factors such as age, iron overload, organ health, the role of allogeneic stem cell transplantation, and the requirements for specialist centres and long term follow up.
Swipe through the carousel for an overview of the recommendations and access the full report here.”
Title 1: Update of the decision-making algorithm on selecting transfusion-dependent β-thalassemic patients for gene therapy approaches: joint consensus report on behalf of EHA-specialized working group and EBMT hemoglobinopathies working party
Authors: Lucia de Franceschi, Mahmoud Aljurf, Donatella Baronciani, Celeste Bento, Christian Chabannon, Selim Corbacioglu, Josu de la Fuente, Gian Luca Forni, Antonis Kattamis, Franco Locatelli, Roland Meisel, Ali Taher, Paul Telfer, Isabelle Thuret, Emanuele Angelucci
Read Full Article on Bone Marrow Transplantation.
Title 2: A long bristling road full of adventure, full of discovery” gene therapy approaches in transfusion-dependent thalassemia: The EHA-EBMT consensus paper
Authors: Lucia De Franceschi, Emanuele Angelucci
Read Full Articles on HemaSphere.
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