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Brian O Mahony on 5-Year Roctavian Gene Therapy Data from BIC2025
Sep 13, 2025, 13:34

Brian O Mahony on 5-Year Roctavian Gene Therapy Data from BIC2025

Brian O Mahony, CEO of Irish Haemophilia Society, Former President of WFH and EHC, shared a post on X:

“Nugent BIC2025 presents 5 year data on valoctocogene roxaparvovec (Roctavian) GENE R-8 1 trial.

128 of 134 participants completed the trial. Using chromogenic assay at 5 years, mean FVIII 13.7, median 6.2 IU/dl 1/3”

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