Brian O Mahony/X
Jun 27, 2025, 16:51
Brian O Mahony: Pipe on 4 Year Data with FIX Gene Therapy (Hemgenix)
Brian O Mahony, Former President of WFH, shared a post on X:
“Pipe on 4 year data with FIX Gene Therapy (Hemgenix).
At year 4, FIX expression :
- 16 at 40-100%
- 27 at 12-40%
- 3 at 5-12%
- 1 at 0-5%
2 initial non responders
1 had liver transplant post HCC
1 RIP from unrelated cause”
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