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Brian O Mahony: Pipe on 4 Year Data with FIX Gene Therapy (Hemgenix)
Jun 27, 2025, 16:51

Brian O Mahony: Pipe on 4 Year Data with FIX Gene Therapy (Hemgenix)

Brian O Mahony, Former President of WFH, shared a post on X:

“Pipe on 4 year data with FIX Gene Therapy (Hemgenix).
At year 4, FIX expression :

  • 16 at 40-100%
  • 27 at 12-40%
  • 3 at 5-12%
  • 1 at 0-5%
    2 initial non responders
    1 had liver transplant post HCC
    1 RIP from unrelated cause”

Brian O Mahony: Pipe on 4 Year Data with FIX Gene Therapy (Hemgenix)

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