Brian O Mahony/X
Jun 24, 2025, 22:08
Rewriting Your DNA in Childhood: Because Why Wait to Cure Hemophilia? | ISTH 2025 Breakthrough
Ben Samelson-Jones, Assistant Professor of Pediatrics at University of Pennsylvania School of Medicine, posted on X:
”Sustained and stable FIX levels have now been repeatedly been observed across multiple #genetherapy clinical trials for Hemophila B. Will extend the red line tomorrow at Clinical Gene Therapy session at ISTH2025.”
Reposting from Brian O Mahony, CEO of the Irish Haemophilia Society and former President of both the WFH and EHC, sharing bold new advances in haemophilia management presented at ISTH 2025 via X:
”FIX expression and durability compared between clinical trials. Malec, ISTH2025.”
Gene Editing: Welcome to a New World!
A shot and you are done with Hemophilia B?
Don’t miss the new updates with Hemostasis Today.
-
Sep 9, 2026, 13:11Ron DePinho: A Negative Trial Does Not Repudiate Inflammation as a Cardiovascular Target
-
Sep 9, 2026, 13:10Ahmad Gharehbaghian: Visiting the Alborz Provincial Blood Transfusion Center
-
Sep 9, 2026, 13:09Oraianthi Fiste: New Collection on Cancer-Associated Thrombosis From Mechanisms to Precision Medicine
-
Sep 9, 2026, 13:07Can Özlü: Can the HALP Score Help Identify Thrombotic Risk in Myeloproliferative Neoplasms?
-
Sep 9, 2026, 13:06Ohanna Cavalcanti Bezerra: Why Does DVT Lead to PE in Some Patients but Not Others?
-
Sep 9, 2026, 13:04Usman Shehzad: Transforming Patient Lives with INR Self-Testing
-
Sep 9, 2026, 13:02Edward Lee Carter: Provoked VTE May Not Tell the Whole Story About Recurrence Risk
-
Sep 9, 2026, 13:01Danielle Charissa: Functional Genomics Reveals a Causal TWIST1 Variant in Cardiovascular Disease
-
Sep 9, 2026, 12:59Hussnain Javaid: MCQ – Based on the Recent BSH’s Guideline on TTP Diagnosis