Brian O Mahony/X
Jun 24, 2025, 22:08
Rewriting Your DNA in Childhood: Because Why Wait to Cure Hemophilia? | ISTH 2025 Breakthrough
Ben Samelson-Jones, Assistant Professor of Pediatrics at University of Pennsylvania School of Medicine, posted on X:
”Sustained and stable FIX levels have now been repeatedly been observed across multiple #genetherapy clinical trials for Hemophila B. Will extend the red line tomorrow at Clinical Gene Therapy session at ISTH2025.”
Reposting from Brian O Mahony, CEO of the Irish Haemophilia Society and former President of both the WFH and EHC, sharing bold new advances in haemophilia management presented at ISTH 2025 via X:
”FIX expression and durability compared between clinical trials. Malec, ISTH2025.”
Gene Editing: Welcome to a New World!
A shot and you are done with Hemophilia B?

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