Wolfgang Miesbach: WFH’s First AAV Gene Therapy Chapter Marks a New Era in Hemophilia Care
Wolfgang Miesbach, Professor of Medicine at Frankfurt University Hospital, shared a post on LinkedIn:
”Treatment for ALL: Diagnosis is rising — but the gap remains vast.
Haemophilia diagnoses climbed to approximately 290,000 (from around 245,000 in 2020) and VWD to around 115,000.
Yet two-thirds of people with haemophilia, and most with VWD (approximately 1 in 1,000), are still undiagnosed.
Humanitarian aid scaled past its target. 34,747 people have now been treated through the programme, including 4,000 children reaching prophylaxis.
The registry became usable.
Past its 10,000-registration target, the new WBDR Data Dashboard lets HTCs and researchers actually interrogate the data — by type, severity, age, and region.
The WFH published its first AAV gene therapy guideline chapter, alongside a shift to a Living Guidelines Model that updates as evidence emerges.
For a field moving this fast, that shift may matter as much as the recommendations themselves.
Behind every number is the WFH‘s core mission: working with NMOs, treatment centres, and healthcare providers worldwide to bring diagnosis and care to everyone with an inherited bleeding disorder — Treatment for ALL.”
Stay updated with Hemostasis Today.
-
Jun 24, 2026, 09:29Advancing Women’s Health Through Collaboration with Jean Hailes for Women’s Health – Stroke Foundation
-
Jun 24, 2026, 09:18The Lasting Immunological Footprint of VITT – JTH
-
Jun 24, 2026, 09:09Umberto Pensato: Dedicated Funding Pathways for Stroke Research in Italy
-
Jun 24, 2026, 09:00Danny Gaskin: BBTS 2026 and the Evolving Role of Transfusion in Maternity Care
-
Jun 24, 2026, 06:42Deepthi Krishna: World Blood Donor Day 2026 Celebrations at Rela Hospital
-
Jun 24, 2026, 03:36Ana Pedrero Gil: A New Approach to Post-Tonsillectomy Hemorrhage
-
Jun 24, 2026, 02:59Melissa Hollo: Making Early Anemia Detection the Standard of Care
-
Jun 24, 2026, 02:51Bruno Pougault: The Thin Line Between Bleeding and Clotting
-
Jun 23, 2026, 23:30Shunsuke Iwano: PMDA Introduces Greater Flexibility for Pediatric Factor VIII and IX Development in Japan